HN Summary
• Gene therapy is shifting medicine from treating symptoms to targeting disease at its genetic source, offering new hope for conditions such as Huntington’s disease, sickle cell disease and inherited neurological disorders.
• Advances in viral delivery systems and gene-editing technologies like CRISPR are accelerating the development of therapies that could slow or even prevent disease progression.
• Canadian researchers and biotechnology companies are playing a leading role in advancing gene therapy research, manufacturing and clinical innovation, with the potential to transform treatment for both rare and common…
